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Acadia Pharmaceuticals USD 1.06B 14.31M 2025-12
Alnylam Pharmaceuticals USD 4.22B 168.65M 2026-03
Amarin USD 626.02M 23.87M 2026-03
BioCryst Pharmaceuticals USD 404.35M 48.66M 2025-12
BioMarin Pharmaceutical USD 4.61B 651.58M 2026-03
DBV Technologies USD 212.94M 124.06M 2025-12
Esperion Therapeutics USD 462.57M 102.11M 2025-12
Galectin Therapeutics USD 27.29M 1.83M 2024-06
Halozyme Therapeutics USD 825.21M 503.54M 2025-12
Incyte USD 5.48B 460.36M 2026-03
Insmed USD 1.79B 137.6M 2025-12
Ionis Pharmaceuticals USD 2.94B 52M 2026-03
Neurocrine Biosciences USD 2.44B 86.6M 2026-03
PTC Therapeutics USD 2.27B 266.14M 2025-12
Sarepta Therapeutics USD 2.54B 184.37M 2025-12
Ultragenyx Pharmaceutical USD 657M 294M 2026-03
United Therapeutics USD 2.87B 830.5M 2026-03